What is one application of gene therapy?

Gene therapy is primarily utilized in the context of treating genetic disorders. This innovative approach involves modifying or manipulating genes to address the underlying causes of these disorders, which often stem from mutations or abnormalities in an individual's DNA. By using techniques such as inserting healthy copies of a gene, repairing defective genes, or even replacing missing genes, gene therapy aims to restore normal function in affected cells or tissues.

This application has tremendous potential and has already been employed in the treatment of various inherited diseases, some types of cancer, and certain viral infections. The focus is on correcting the specific genetic defects that lead to the clinical manifestations of these conditions, thus providing a more effective and targeted method of treatment compared to traditional therapies.